Publications scientifiques 2010

1. Toromanoff A, Adjali O, Larcher T, Hill M, Guigand L, Chenuaud P, Deschamps JY, Gauthier O, Blancho G, Vanhove B, Rolling F, Chérel Y, Moullier P, Anegon I, Le Guiner C. Lack of immunotoxicity after regional intravenous (RI) delivery of rAAV to nonhuman primate skeletal muscle. Mol Ther. 2010 18(1) : 151-160

2. Colle MA, Piguet F, Bertrand L, Raoul S, Bieche I, Dubreil L, Sloothaak D, Bouquet C, Moullier P, Aubourg P, Cherel Y, Cartier N, Sevin C. Efficient intracerebral delivery of AAV5 vector encoding human arsa in non-human primate. Hum Mol Genet. 2010. 19(1) :147-158

3. Lhériteau E, Libeau L, Mendes-Madeira A, Deschamps JY, Weber M, Le Meur G, Provost N, Guihal C, Moullier P, Rolling F. Regulation of Retinal Function but Nonrescue of Vision in RPE65-deficient Dogs Treated With Doxycycline-regulatable AAV Vectors. Mol Ther. 2010 Jun ;18(6) :1085-93.Epub 2010 Mar 30.

4. Lock M, McGorray S, Auricchio A, Ayuso E, Beecham EJ, Blouin-Tavel V, Bosch F, Bose M, Byrne BJ, Caton T, Chiorini JA, Chtarto A, Clark KR, Conlon T, Darmon C, Doria M, Douar A, Flotte TR, Francis JD, Francois A, Giacca M, Korn MT, Korytov I, Leon X, Leuchs B, Lux G, Melas C, Mizukami H, Moullier P, Müller M, Ozawa K, Philipsberg T, Poulard K, Raupp C, Rivière C, Roosendaal SD, Samulski RJ, Soltys SM, Surosky R, Tenenbaum L, Thomas DL, van Montfort B, Veres G, Wright JF, Xu Y, Zelenaia O, Zentilin L, Snyder RO. Characterization of a Recombinant Adeno-Associated Virus Type 2 Reference Standard Material. Human Gene Therapy, 2010 Oct;21(10):1273-85.

5. Ellinwood NM, Ausseil J, Desmaris N, Bigou S, Liu S, Jens JK, Snella EM, Mohammed EE, Thomson CB, Raoul S, Joussemet B, Roux F, Chérel Y, Lajat Y, Piraud M, Benchaouir R, Hermening S, Petry H, froissard R, Tardieu M, Ciron C, Moullier P, Parkes J, Kline KL, Maire I, Vanier MT, Heard JM, Colle MA. Safe, efficient, and reproductible gene therapy of the brain in the dog models of Sanfilippo and Hurler syndromes. Mol Ther.2011 Feb ;19(2) :251-9 Epub 2010 Dec 7

6. Stieger K, Chauveau C, Rolling F. Preclinical studies on specific gene therapy for recessive retinal degenerative diseases. Cur Gene Ther.2010 Oct ;10(5) :389-403

7. Rolling F. AAV mediated gene therapy for the treatment of retinal diseases. Curr Gene Ther.2010 Oct

8. Abarrategui-Pontes, C., Podevin, G., Schmitt, F., Dariel, A., Pichard, V., Boni, S., Deschamps, J.Y., Cherel, Y., Babarit, C., Badaud, C., Delanoe, N., Fouassier, M., Ferry, N., Tuan, H.N., 2010, Feasibility and Biosafety of an In Vivo Liver Gene Therapy Approach in Nonhuman Primates. Human Gene Therapy 21, 781-781.

9. Heard, J.M., Vitry, S., Bruyre, J., Hocquemiller, M., Bigou, S., Nosjean, A., Ausseil, J., Colle, M.A., Pruvost, M.C., 2010, Abnormal vacuoles distinct from lysosomes in a mouse model of mucopolysaccharidosis type IIIB. Molecular Genetics and Metabolism 99, 58.

10. Labadie, K., Larcher, T., Joubert, C., Mannioui, A., Delache, B., Brochard, P., Guigand, L., Dubreil, L., Lebon, P., Verrier, B., de Lamballerie, X., Suhrbier, A., Cherel, Y., Le Grand, R., Roques, P., 2010, Chikungunya disease in nonhuman primates involves long-term viral persistence in macrophages. Journal of Clinical Investigation 120, 894-906.

11. Laurent, S., Sabot, A.S., Colle, M.A., Nicolier, A., 2010, LYSOSOMAL STORAGE DISEASE IN TWO PRESUMED-RELATED SPRINGBOKS (ANTIDORCAS MARSUPIALIS). Journal of Zoo and Wildlife Medicine 41, 104-110.

12. Laurent, S., Thibaud, J.L., Hordeaux, J., Reyes-Gomez, E., Delisle, F., Blot, S., Colle, M.A., 2010, Chronic Traumatic Brain Injury in a Dog. J. Comp. Pathol. 143, 75-80.

13. Lheriteau, E., Libeau, L., Mendes-Madeira, A., Deschamps, J.Y., Weber, M., Le Meur, G., Provost, N., Guihal, C., Moullier, P., Rolling, F., 2010, Regulation of Retinal Function but Nonrescue of Vision in RPE65-deficient Dogs Treated With Doxycycline-regulatable AAV Vectors. Molecular Therapy 18, 1085-1093.

14. Merceron, C., Portron, S., Masson, M., Fellah, B.H., Gauthier, O., Lesoeur, J., Cherel, Y., Weiss, P., Guicheux, J., Vinatier, C., 2010, Cartilage tissue engineering: From hydrogel to mesenchymal stem cells. Bio-Medical Materials and Engineering 20, 159-166.

15. Mondoulet, L., Dioszeghy, V., Ligouis, M., Dhelft, V., Larcher, T., Cherel, Y., Dupont, C., Benhamou, P., 2010, A Model of Eosinophilic Esophagitis (EE) and Villus Atrophy (VA) after Challenge in Mice Sensitized to Peanuts: Improvement by Epicutaneous Immunotherapy (EPIT). Journal of Allergy and Clinical Immunology 125, AB161-AB161.

16. Munier, S., Larcher, T., Cormier-Aline, F., Soubieux, D., Su, B., Guigand, L., Labrosse, B., Cherel, Y., Quere, P., Marc, D., Naffakh, N., 2010, A Genetically Engineered Waterfowl Influenza Virus with a Deletion in the Stalk of the Neuraminidase Has Increased Virulence for Chickens. Journal of Virology 84, 940-952.

17. Piguet, F., Sondhi, D., Colle, M.A., Raoul, S., Roujeau, T., Piraud, M., Ahouansou, O., Bouquet, C., Vanier, M.T., Moullier, P., Cherel, Y., Hackett, N.R., Zerah, M., Aubourg, P., Crystal, R.G., Cartier, N., Sevin, C., 2010, Brain Gene Therapy for Metachromatic Leukodystrophy: Towards Clinical Trial. Human Gene Therapy 21, 771-771.

18. Morille M, Montier T, Legras P, Carmoy N, Brodin P, Pitard B, Benoît JP, Passirani C. Long-circulating DNA lipid nanocapsules as new vector for passive tumor targeting. Biomaterials. (2010) 31:321-9

19. Labas R, Beilvert F, Barteau B, David S, Chèvre R, Pitard B. Nature as a source of inspiration for cationic lipid synthesis. Genetica. (2010) 138:153-68.